The Pipeline Blog

In The Pipeline Blog, we aim to discuss a variety of medical and regulatory affairs topics.

  • Kebilidi

    Author: Michaela Price, PhD Editors: Morgan McCullough & Kylie VanDerMolen Today, we will be discussing Kebilidi (eladocagene exuparvovec-tneq). Kebilidi is manufactured by PTC Therapeutics, Inc. and was approved for the treatment of aromatic L-amino acid decarboxylase (AADC) deficiency. In the … Read more

  • Gene Therapies for Sickle Cell Disease

    Author: Kylie VanDerMolen  Editors: Morgan McCullough and Michaela Price, PhD  Today, we will be covering the landmark Food and Drug Administration (FDA)-approvals of the first gene therapies to treat sickle cell disease. On December 8, 2023, the FDA approved Casgevy … Read more

  • Kinase Inhibitors in Cancer

    Authors: Chip Norwood & Oleg Kolupaev Today, we are here with another post covering kinase inhibitors specifically related to cancer. We will cover several topics within this post, including: 1) the impact of cancer on human health, 2) a general … Read more

  • Remdesivir

    Authors: Chip Norwood & Oleg Kolupaev Today, our first-ever The Pipeline Blog post will cover the antiviral drug Remdesivir. This therapeutic has received a lot of attention from the media and researchers across the globe to treat COVID-19. Herein, we … Read more